Has gene therapy for als arrived?

Amyotrophic lateral sclerosis has not responded well in clinical trials to what initially seemed a promising therapy—the administration of neuronal growth and survival factors. Now, a gene

therapy-based approach in mice revives hope that proper delivery of such factors can slow the disease's course. Access through your institution Buy or subscribe This is a preview of

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ADDITIONAL ACCESS OPTIONS: * Log in * Learn about institutional subscriptions * Read our FAQs * Contact customer support REFERENCES * Elliott, J.L. & Snider, W.D. _Neurology_ 47,

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AUTHOR INFORMATION AUTHORS AND AFFILIATIONS * Department of Neurosciences and the Ludwig Institute for Cancer Research, Timothy M Miller & Don W Cleveland * Departments of Neurosciences,

Medicine, and Cellular and Molecular Medicine and the Ludwig Institute for Cancer Research, University of California at San Diego, 9500 Gilman Drive, La Jolla, 92093-0670, California, USA

Timothy M Miller & Don W Cleveland Authors * Timothy M Miller View author publications You can also search for this author inPubMed Google Scholar * Don W Cleveland View author

publications You can also search for this author inPubMed Google Scholar RIGHTS AND PERMISSIONS Reprints and permissions ABOUT THIS ARTICLE CITE THIS ARTICLE Miller, T., Cleveland, D. Has

gene therapy for ALS arrived?. _Nat Med_ 9, 1256–1257 (2003). https://doi.org/10.1038/nm1003-1256 Download citation * Issue Date: 01 October 2003 * DOI: https://doi.org/10.1038/nm1003-1256

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